This chapter discusses trials in which gene therapy is used to treat ornithine transcarbamylase deficiency. The studies covered include the use of gene therapy in male infants under nine years of age as well as research on mediated gene transfers.

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Ornithine Transcarbamylase Deficiency

  • Jeffrey N. Weiss

摘要

This chapter discusses trials in which gene therapy is used to treat ornithine transcarbamylase deficiency. The studies covered include the use of gene therapy in male infants under nine years of age as well as research on mediated gene transfers.