This chapter discusses trials in which gene therapy is used to treat patients with adrenoleukodystrophy. Adrenoleukodystrophy, or ALD, is a rare, genetic disorder primarily affecting the nervous system.

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Adrenoleukodystrophy

  • Jeffrey N. Weiss

摘要

This chapter discusses trials in which gene therapy is used to treat patients with adrenoleukodystrophy. Adrenoleukodystrophy, or ALD, is a rare, genetic disorder primarily affecting the nervous system.