Scholarlink

This chapter discusses trials in which gene therapy is used to treat Friedreich’s ataxia. The trials include the use of gene therapy to treat cardiomyopathy of Friedreich’s ataxia as well as adults who have heart disease in association with Friedreich’s ataxia.

错误：搜索内容不能为空，请输入英文关键词
错误：关键词超出字数限制，请精简
高级检索

Friedreich’s Ataxia

  • 章节

  • 发表日期：

    2025年

查看全文
  • Jeffrey N. Weiss

摘要

This chapter discusses trials in which gene therapy is used to treat Friedreich’s ataxia. The trials include the use of gene therapy to treat cardiomyopathy of Friedreich’s ataxia as well as adults who have heart disease in association with Friedreich’s ataxia.